WWOX

First-of-its-kind experimental gene therapy administered at Schneider Children's Center to a baby with WOREE syndrome, a rare disease caused by a defect in the WWOX gene. Credit: Hebrew University / Schneider Children's Center.

For the first time: Experimental WWOX gene therapy injected into the brain of a baby with severe genetic epilepsy

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Conceptual illustration of an AAV9 vector that delivers the WWOX gene to nerve cells in the brain as part of experimental gene therapy for WOREE syndrome.
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